Ionis Pharmaceuticals

74.79
Open
73.74
Market Cap
12.35B+
High
75.13
Low
73.35
Close
74.79
Volume
1.79M+
P/E Ratio
-31.42
Div/Yield
0.00%

About Ionis Pharmaceuticals

Ionis Pharmaceuticals, Inc. 在美國發現和開發 RNA 靶向療法。該公司為兒童和成人患者的脊髓性肌萎縮症(SMA)提供 SPINRAZA; TEGSEDI,一種用於治療成人遺傳性轉甲狀腺素蛋白介導的澱粉樣變性多發性神經病的注射劑;和 WAYLIVRA,一種治療家族性乳糜微粒血症綜合徵和家族性部分脂肪代謝障礙的藥物。它還針對處於 3 期研究的各種適應症開發藥物,包括 Eplontersen 作為每月自我管理的皮下注射劑來治療所有類型的 TTR 澱粉樣變性; Olezarsen 用於嚴重高甘油三酯血症 (SHTG) 患者; Donidalorsen 用於遺傳性血管性水腫患者; ION363 用於肌萎縮側索硬化患者; Pelacarsen 用於已確診心血管疾病和脂蛋白 (a) 升高的患者;和 Tofersen 抑制超氧化物歧化酶 1 的產生。此外,該公司還開髮用於代謝疾病、傳染病、腎臟疾病、眼科疾病和癌症的藥物。與Biogen Inc.達成戰略合作;以及與 AstraZeneca、Bayer AG、GlaxoSmithKline plc、Novartis AG、Roche、Janssen Biotech, Inc. 和 Flamingo Therapeutics, Inc. 的合作和許可協議。Ionis Pharmaceuticals, Inc. 成立於 1989 年,總部位於加利福尼亞州卡爾斯巴德。

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